Cure SMA Breaking News
no more sma angels
Two significant FDA approved treatments are changing the course of SMA.
MAY 2019 - FDA APPROVES ZOLGENSMA
AveXis Receives FDA Approval of Zolgensma, a Gene Therapy, for Spinal Muscular Atrophy for Patients Under Two Years of Age.
DECEMBER 2016 - FDA APPROVES SPINRAZA
On December 23, 2016, the FDA approved Spinraza (nusinersen) to treat Spinal Muscular Atrophy, making it the first-ever FDA-approved therapy for SMA.